Gene therapies to treat rheumatoid arthritis have evolved slowly, but one is ready to move into human trials and an ...

Broken String Biosciences ("Broken String"), a leader in advancing gene editing safety, today opened its Catalyst Early ...

The FDA approved betibeglogene autotemcel (beti-cel; Zynteglo) for adult and pediatric patients with transfusion-dependent ...

NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...

Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

The UK has approximately 17,500 individuals living with sickle cell disease, a condition particularly prevalent amongst those ...

International collaborations, refined gene-editing protocols, and targeted immunologic maneuvers keep the cancer gene therapy ...

This new on-demand offering enables gene editing therapy developers to assess on- and off-target effects in days, as opposed to months. The offering can be integrated into early therapeutics ...

A gene-editing therapy for sickle cell disease, with a price tag of £1.65m, is to be offered to patients on the NHS in ...