Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude ...

Members of the St. Mary’s Academy U18 prep hockey team are playing with heavy hearts following news the school has shuttered ...

This rare genetic disorder was just treated in the womb for the first time ever - Without treatment, those with the more ...

Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...

On the upside, the first hurdle is the 2025 high of 0.6395 (February 20). The next level to watch is the 100-day Simple Moving Average (SMA) at 0.6425, followed by the weekly top at 0.6549 (November ...

The first prenatal therapy for spinal muscular atrophy (SMA) showed promising results, a case report indicated. More than 2 ...

Doctors diagnosed Carmen Lopez with spinal muscle atrophy (SMA) at birth, a rare genetic disorder that affects motor neurons ...

Stax Music Academy will mark its anniversary with concerts and educational efforts, including “Soul of America,” a virtual ...

February is Rare Disease Awareness month. The upcoming week has been declared Rare Disease Awareness week, with Rare Disease ...

The U.S. Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for ...

The spot gold price is trading at record highs and targets the psychological $3000 mark amid flight-to-safety inflows due to ...