Researchers are enhancing the best features of AAV capsids and overcoming their limitations to accelerate gene-based therapies.
FDA aligned on single-arm Phase 3 study to support potential accelerated and full approvalOn track to dose first patient in Phase 3 trial in ...
A new, streamlined AAV purification process that is both universal and scalable could ease commercialization constraint.
These DNA viruses in the family Adenoviridae are frequently accompanied by small, single-stranded DNA parvoviruses known as adeno-associated viruses, that don't seem to cause any specific disease.
This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...
The majority are in the very early preclinical stage of development, but applications for regulatory approval have been ...
Some gene therapy treatments use modified adeno-associated viruses (AAVs) like the one shown here to deliver therapeutic genetic material into a patient’s cells. In a finding with implications ...