St. Louis American12h
Wash U student study explores sickle cell impact on thinking
In addition to the prolonged pain and suffering endured by sickle cell patients, a Washington University School of Medicine study has concluded that there could be a significant impact on cognitive ...
Gene variant could protect against ultra-rare seizure disorder, fruit fly research finds
One in 10 Americans live with a rare disease, which often lacks effective treatments. Such is the case for PIGA-CDG, an ultra ...
Medscape1d
Sickle Cell Trait Widely Misinterpreted As Cause of Death
A new review and policy statement underscore the inaccuracy of sickle cell trait as a cause of death on autopsies.
Hosted on MSN2d
Cherokee County man cured of sickle cell anemia complications at Atlanta hospital, he says
Kyle Registre's childhood dream of becoming a pilot can finally come true now that he says he's been cured of sickle cell ...
KTBS2d
Texarkana boy battling rare disease prepares for life-changing transplant
TEXARKANA, Texas - A Texarkana, Texas boy battling a rare genetic disease is preparing to head to Arkansas Children's ...
The Punch on MSN10d
Groundbreaking sickle cell disease treatment approved for English NHS
Sickle cell anaemia is a genetic blood disorder characterised by the production of an abnormal haemoglobin, known as haemoglobin S. Sickle cell disease changes the shape of blood cells into a crescent ...
Sky14d
'Groundbreaking' sickle cell treatment to be offered to NHS patients for first time
A "groundbreaking" £1.65 million treatment has been approved for use on the NHS, offering patients with severe sickle cell disease some hope of a cure. It is believed around 1,700 people could be ...
National Institute for Health and Care Excellence14d
Groundbreaking one-off gene therapy approved for severe sickle cell disease
Our independent appraisal committee has approved the use of gene editing therapy exagamglogene autotemcel (exa-cel) for use in the NHS in England, providing a potential cure for some people with ...
AOL.co.uk14d
Sickle cell patients share delight over approval of new treatment
A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle cell disease. Casgevy, also known as exa-cel, was the first treatment to be licensed using gene ...
The Daily Telegraph14d
Sickle cell disease ‘cure’ to be offered to NHS patients
A sickle cell disease “cure” is to be offered to NHS patients for the first time. The £1.65 million gene therapy called exa-cel, also known under the brand name Casgevy, uses a Nobel Prize ...
Channel 4 News14d
Sickle cell disease: new treatment raises hopes of cure for sufferers
Would it be a cure for my sickle cell disease? It was a decision I could think about making because my sister was a genetic match and could donate her stem cells. Most with sickle cell don’t ...
Reuters14d
UK health system to offer cutting-edge gene therapy for sickle cell disease
LONDON, Jan 31 (Reuters) - Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the National Institute for Health and Care ...