The drug is the first non-cannabinoid option for patients with LGS and an alternative to Jazz Pharma's Epidyolex (cannabidiol ...

Hundreds of children with severe epilepsy will be able to benefit from a groundbreaking new treatment on the NHS that could significantly reduce their seizures, providing new hope for them and their ...

However, we still see areas of weakness in the portfolio, including upcoming patent losses and a highly uncertain pipeline due to the complexities of running CNS trials. Historically, the firm ...

With only a few exceptions, these drugs were discovered by screening ... of action of lacosamide (Vimpat), a recently approved antiepileptic drug, and the mechanisms by which some antiseizure ...

Ultragenyx Pharmaceutical RARE reported new findings from an ongoing, pivotal study of its investigational candidate, UX111 (ABO-102) AAV gene therapy, for Sanfilippo syndrome type A (MPS IIIA).

People will have their drug of choice, whether it’s shopping or social media or video games or pornography. But if that’s not available, they’ll switch to something else. That timeline is ...

These DEEs included Dravet syndrome (n=3), Lennox-Gastaut syndrome (n=20), and other (n=18). PACIFIC OLE is a 52-week open-label, long-term safety trial conducted at 34 sites across the United States ...

PARIS, Jan 30 (Reuters) - Forty-five people have been arrested in west Africa over the past three months in operations targeting drugs trafficking and the financing of terrorism, said global ...

For Dravet syndrome and Lennox-Gastaut syndrome, Epidyolex must be used alongside the epilepsy medicine, clobazam. NICE says doctors should check the frequency of seizures every 6 months, and stop ...

Top doctors raised concerns about domestically made drugs, saying Beijing’s effort to lower costs is sacrificing quality. By Alexandra Stevenson and Zixu Wang Reporting from Hong Kong A rare ...