Biogen receives exclusive rights to commercialize zorevunersen outside U.S., Europe, and Japan.

AAV-Navβ1 gene therapy effectively reduces seizures and prolongs life in a mouse model of SCN1B-linked Dravet syndrome, ...

Encoded Therapeutics is shrinking its headcount by 29% as the gene therapy biotech draws resources away from its early-stage ...

However, we still see areas of weakness in the portfolio, including upcoming patent losses and a highly uncertain pipeline due to the complexities of running CNS trials. Historically, the firm ...

Turner syndrome is a rare genetic disorder found in some women and people assigned female at birth. It can cause short stature and a range of health issues including heart defects, learning ...

It's official. Triple H is getting his long overdue induction into the WWE Hall of Fame. The news was first broken by several outlets Wednesday afternoon, and then officially announced by WWE ...

A 40-year-old man suspected of having Guillain-Barre Syndrome (GBS) died in Solapur, Maharashtra. Over 100 cases of GBS have been reported in Pune. The syndrome, often triggered by bacterial and viral ...

What is Zollinger-Ellison syndrome? Zollinger-Ellison syndrome (ZES) is a rare digestive disorder. If you have ZES, you likely have 1 or more tumors in the first part of the small intestine, the ...

The proposed study will evaluate two loading doses of 70mg followed by two maintenance doses of 45mg over 52-weeks compared to sham in children and adolescents ages 2 to <18 with Dravet syndrome.

Prenatal testing for Down syndrome can help you understand your baby’s development before birth and provide information to guide your pregnancy journey. Read on to learn more about prenatal ...