SMA10h
Child doing well after mother had SMA treatment while pregnant
A mother was given SMA treatment Evrysdi during pregnancy, and her child with SMA, now 2.5, has not shown any signs of the ...
Neurology Advisor12h
FDA Approves Tablet Form of Evrysdi for Spinal Muscular Atrophy
The US Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for people living with spinal muscular atrophy (SMA).
New Atlas20h
Infant's genetic muscle disorder improved by treating pregnant mother
Spinal muscular atrophy (SMA) is a debilitating genetic condition that’s usually fatal by a few years of age. But an ...
The American Journal of Managed Care11h
Redefining Functional Measures in SMA: Insights From Clinical Research
The evolution of functional assessments for spinal muscular atrophy (SMA) highlights the challenges of adapting pediatric ...